Improved Medication – Pilot Study Underway

Pilot Study Comparing Cysteamine Bitartrate Delayed-release Capsules (RP103) Cysteamine Bitartrate Capsules, (Cystagon) is Underway

 

 

A pilot study is currently underway at the University of California, San Diego (UCSD). This pilot study is comparing an investigational cysteamine drug (RP103) for the potential treatment of cystinosis to the existing treatment, Cystagon®. Dr. Bruce Barshop is the principal investigator for this study.

 

Through this work we are learning some important things about dose and administration of the investigational drug RP103. Before moving on to the phase 3 study, it is important to better understand how best to administer the Cysteamine Bitartrate Delayed-release Capsules.  Raptor Pharmaceuticals has submitted the Investigational Drug Application, and anticipates submitting the New Drug Application after phase 3 trials are completed.

More information is available at clinicaltrials.gov.

Raptor Pharmaceuticals is sponsoring this study. It is the first clinical study planned with Cysteamine Bitartrate Delayed-release Capsules.

 

 

Participation in research is always entirely voluntary. If you are interested in participating and would like more information, please contact Betty Cabrera B.S., M.P.H.  at University of California San Diego Medical Center, San Diego, California, United States, 92103. Phone: (619) 471-9554 or email: blcabrera@ucsd.edu.

 

 


Save the Date for Natalie’s Wish Fundraiser– April 30th at the Balboa Bay Club, Newport Beach, CA
John Ondrasik

Join us Friday, April 30th for our annual Natalie’s Wish fundraising event at the beautiful Balboa Bay Club in Newport Beach, CA. Guests will enjoy a live performance by John Ondrasik of Five for Fighting, and a short film on cystinosis research progress. Then the bidding begins on fabulous items in our live auction, including fantastic travel and entertainment packages, jewelry and wine collections. This event is the highlight of our year, with many of our supporters and cystinosis families joining together for a night of hope and celebration in our quest to cure cystinosis. More information and invitations to come.

Join our mailing list by emailing info@cystinosisresearch.org with your contact information.